{"id":7289,"date":"2022-02-09T09:01:00","date_gmt":"2022-02-09T09:01:00","guid":{"rendered":"https:\/\/factor-h.org\/?p=7289"},"modified":"2022-02-09T09:01:00","modified_gmt":"2022-02-09T09:01:00","slug":"2021-course-on-targeting-mutant-htt-therapeutically-for-clinicians-of-the-movement-disorder-society-mds-by-ignacio-munoz-sanjuan","status":"publish","type":"post","link":"https:\/\/factor-h.org\/es\/2021-course-on-targeting-mutant-htt-therapeutically-for-clinicians-of-the-movement-disorder-society-mds-by-ignacio-munoz-sanjuan","title":{"rendered":"2021 Curso para especialistas de la sociedad de trastornos del movimiento (MDS) sobre terapias experimentales para la enfermedad de Huntington, por Ignacio Mu\u00f1oz-Sanjuan"},"content":{"rendered":"<p>En este curso 2021, el Dr. Ignacio Mu\u00f1oz-Sanjuan, VP de biolog\u00eda traslacional de la Fundaci\u00f3n CHDI, habla a los m\u00e9dicos y residentes de trastornos del movimiento como parte de un curso sobre la enfermedad de Huntington organizado por EHDN y MDS. <\/p>\n\n\n\n<p>El seminario se centra en nuestra comprensi\u00f3n actual de los aspectos biol\u00f3gicos de HTT relevantes para el desarrollo de terapias dirigidas a la causa de la enfermedad, el gen mutante de la Huntingtina (HTT), a trav\u00e9s de varios enfoques, que incluyen mol\u00e9culas peque\u00f1as, oligonucle\u00f3tidos antisentido (ASO) y genes dirigidos a ARNm. agentes de terapia administrados a trav\u00e9s de virus adenoasociados (AAV). <\/p>\n\n\n\n<p>Ignacio describe los desaf\u00edos biol\u00f3gicos, tecnol\u00f3gicos y m\u00e9dicos actuales en la realizaci\u00f3n de estudios terap\u00e9uticos para reducir el mHTT, y se centra en el presente y el futuro de esta \u00e1rea de investigaci\u00f3n esencial para desarrollar terapias efectivas para la EH. Es un curso repleto de informaci\u00f3n importante sobre los ensayos en curso y el trabajo para demostrar que es probable que este enfoque sea eficaz para retrasar la progresi\u00f3n de la enfermedad.<\/p>\n\n\n\n<p><span style=\"text-decoration: underline\" class=\"underline\">La charla ha sido aprobada para divulgaci\u00f3n p\u00fablica por MDS y EHDN<\/span> a trav\u00e9s del sitio web de Factor-H, por lo que estamos agradecidos. <\/p>\n\n\n\n<p>Compartir informaci\u00f3n es fundamental para mantener informada y activa a la comunidad de la EH.<\/p>\n\n\n\n<p>Disfrutar.<\/p>\n\n\n\n<figure class=\"wp-block-embed is-type-video is-provider-youtube wp-block-embed-youtube wp-embed-aspect-16-9 wp-has-aspect-ratio\"><div class=\"wp-block-embed__wrapper\">\n<iframe title=\"Ignacio Munoz-Sanjuan 2021 course on Huntington&#039;s disease for MDS and EHDN clinicians and residents\" width=\"800\" height=\"450\" src=\"https:\/\/www.youtube.com\/embed\/q549nEyOrk8?feature=oembed\" frameborder=\"0\" allow=\"accelerometer; autoplay; clipboard-write; encrypted-media; gyroscope; picture-in-picture\" allowfullscreen><\/iframe>\n<\/div><\/figure>","protected":false},"excerpt":{"rendered":"<p>In this 2021 course, Dr. Ignacio Munoz-Sanjuan, VP of translational biology at CHDI Foundation, speaks to the clinicians and movement disorder residents as part of a course about Huntington&#8217;s disease organized by EHDN and MDS. The seminar focuses on our current understanding of HTT biological aspects relevant to the development of therapeutics targeting the cause [&hellip;]<\/p>\n","protected":false},"author":4,"featured_media":7290,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"footnotes":""},"categories":[105,9,29],"tags":[162,161,157,160,158,149,151,156,159,155],"class_list":["post-7289","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-for-the-press","category-general-news","category-research","tag-aso","tag-drug-discovery","tag-ehdn","tag-gene-therapy","tag-hd","tag-htt","tag-huntingtons","tag-mds","tag-munoz-sanjuan","tag-seminar-2"],"aioseo_notices":[],"_links":{"self":[{"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/posts\/7289","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/users\/4"}],"replies":[{"embeddable":true,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/comments?post=7289"}],"version-history":[{"count":0,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/posts\/7289\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/media\/7290"}],"wp:attachment":[{"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/media?parent=7289"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/categories?post=7289"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/factor-h.org\/es\/wp-json\/wp\/v2\/tags?post=7289"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}