{"id":7289,"date":"2022-02-09T09:01:00","date_gmt":"2022-02-09T09:01:00","guid":{"rendered":"https:\/\/factor-h.org\/?p=7289"},"modified":"2022-02-09T09:01:00","modified_gmt":"2022-02-09T09:01:00","slug":"2021-course-on-targeting-mutant-htt-therapeutically-for-clinicians-of-the-movement-disorder-society-mds-by-ignacio-munoz-sanjuan","status":"publish","type":"post","link":"https:\/\/factor-h.org\/pt\/2021-course-on-targeting-mutant-htt-therapeutically-for-clinicians-of-the-movement-disorder-society-mds-by-ignacio-munoz-sanjuan","title":{"rendered":"2021 Curso de segmenta\u00e7\u00e3o mutante HTT terapeuticamente para cl\u00ednicos de dist\u00farbio de movimento da sociedade (MDS) por Ignacio Mu\u00f1oz-san juan"},"content":{"rendered":"<p>Neste curso de 2021, o Dr. Ignacio Munoz-Sanjuan, vice-presidente de biologia translacional da Funda\u00e7\u00e3o CHDI, fala aos m\u00e9dicos e residentes de dist\u00farbios do movimento como parte de um curso sobre a doen\u00e7a de Huntington organizado pela EHDN e MDS. <\/p>\n\n\n\n<p>O semin\u00e1rio enfoca nossa compreens\u00e3o atual dos aspectos biol\u00f3gicos do HTT relevantes para o desenvolvimento de terapias direcionadas \u00e0 causa da doen\u00e7a, o gene mutante Huntingtin (HTT), por meio de v\u00e1rias abordagens, incluindo pequenas mol\u00e9culas, oligonucleot\u00eddeos antisense (ASOs) e gene de direcionamento de mRNA agentes de terapia entregues via v\u00edrus adeno-associados (AAVs). <\/p>\n\n\n\n<p>Ignacio descreve os atuais desafios biol\u00f3gicos, tecnol\u00f3gicos e m\u00e9dicos na condu\u00e7\u00e3o de estudos terap\u00eauticos de redu\u00e7\u00e3o do mHTT e enfoca o presente e o futuro desta \u00e1rea de pesquisa essencial para o desenvolvimento de terapias eficazes para a DH. \u00c9 um curso cheio de informa\u00e7\u00f5es importantes sobre ensaios em andamento e trabalho para demonstrar que essa abordagem provavelmente ser\u00e1 eficaz em retardar a progress\u00e3o da doen\u00e7a,<\/p>\n\n\n\n<p><span style=\"text-decoration: underline\" class=\"underline\">A palestra foi aprovada para divulga\u00e7\u00e3o p\u00fablica pelo MDS e EHDN<\/span> atrav\u00e9s do site da Factor-H, e por isso continuamos gratos. <\/p>\n\n\n\n<p>Compartilhar informa\u00e7\u00f5es \u00e9 fundamental para manter a comunidade HD informada e ativa.<\/p>\n\n\n\n<p>Aproveitar.<\/p>\n\n\n\n<figure class=\"wp-block-embed is-type-video is-provider-youtube wp-block-embed-youtube wp-embed-aspect-16-9 wp-has-aspect-ratio\"><div class=\"wp-block-embed__wrapper\">\n<iframe title=\"Ignacio Munoz-Sanjuan 2021 course on Huntington&#039;s disease for MDS and EHDN clinicians and residents\" width=\"800\" height=\"450\" src=\"https:\/\/www.youtube.com\/embed\/q549nEyOrk8?feature=oembed\" frameborder=\"0\" allow=\"accelerometer; autoplay; clipboard-write; encrypted-media; gyroscope; picture-in-picture\" allowfullscreen><\/iframe>\n<\/div><\/figure>","protected":false},"excerpt":{"rendered":"<p>In this 2021 course, Dr. Ignacio Munoz-Sanjuan, VP of translational biology at CHDI Foundation, speaks to the clinicians and movement disorder residents as part of a course about Huntington&#8217;s disease organized by EHDN and MDS. The seminar focuses on our current understanding of HTT biological aspects relevant to the development of therapeutics targeting the cause [&hellip;]<\/p>\n","protected":false},"author":4,"featured_media":7290,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"footnotes":""},"categories":[105,9,29],"tags":[162,161,157,160,158,149,151,156,159,155],"class_list":["post-7289","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-for-the-press","category-general-news","category-research","tag-aso","tag-drug-discovery","tag-ehdn","tag-gene-therapy","tag-hd","tag-htt","tag-huntingtons","tag-mds","tag-munoz-sanjuan","tag-seminar-2"],"aioseo_notices":[],"_links":{"self":[{"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/posts\/7289","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/users\/4"}],"replies":[{"embeddable":true,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/comments?post=7289"}],"version-history":[{"count":0,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/posts\/7289\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/media\/7290"}],"wp:attachment":[{"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/media?parent=7289"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/categories?post=7289"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/factor-h.org\/pt\/wp-json\/wp\/v2\/tags?post=7289"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}