We are honored to be 1 of 5 finalist nonprofit organizations being nominated for this prestigious award, selected out of 90 applicant organizations. The award
Yesterday, Uniqure reported on the 24-month results of their Phase 1/2 clinical trial with AMT-130, a viral gene therapy trial for HTT lowering for the
From a gene mutation to a lethal disease HD is caused by a single mutation in a region of the HTT gene, located at the
Dilia Oviedo Güillín, a woman of unwavering spirit and strength, always dreamed of reuniting her deceased husband and children in a place where they could
Team work and scientific education Every year, Factor-H Vice President Roger Cachope and I visit the Colombian & Venezuelan communities at least once, and over
Factor-H offers a free-of-charge legal assistance service in Colombia, with the sole objective of facilitating access to the services, medicines and supplies that the Colombian
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